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Neurovascular Involvement in Arterial Tortuosity Syndrome Associated with a Homozygous SLC2A10 p.(Trp162Ter) Variant: Clinical, Molecular, and In Silico Characterization.

Neurovascular Involvement in Arterial Tortuosity Syndrome Associated with a Homozygous SLC2A10 p.(Trp162Ter) Variant: Clinical, Molecular, and In Silico Characterization.

期刊: International journal of molecular sciences 日期: 2026-07-29 PMID: 42589462 DOI: 10.3390/ijms27156806 浏览: 7
作者: Bozlak S, Yavas C, Yalcin E, Seflekci Y, Dogan T, Ece A, Akyel NG, Yuksel A
S, B., C, Y., E, Y., Y, S., T, D., A, E., NG, A., & A, Y. (2026). Neurovascular Involvement in Arterial Tortuosity Syndrome Associated with a Homozygous SLC2A10 p.(Trp162Ter) Variant: Clinical, Molecular, and In Silico Characterization.. International journal of molecular sciences. https://doi.org/10.3390/ijms27156806
S B, C Y, E Y, Y S, T D, A E, et al. Neurovascular Involvement in Arterial Tortuosity Syndrome Associated with a Homozygous SLC2A10 p.(Trp162Ter) Variant: Clinical, Molecular, and In Silico Characterization.. International journal of molecular sciences. 2026; doi: 10.3390/ijms27156806
S B, C Y, E Y, et al. Neurovascular Involvement in Arterial Tortuosity Syndrome Associated with a Homozygous SLC2A10 p.(Trp162Ter) Variant: Clinical, Molecular, and In Silico Characterization.[J]. International journal of molecular sciences. 2026. DOI: 10.3390/ijms27156806.
@article{s2026,
  author = {Bozlak S and Yavas C and Yalcin E and Seflekci Y and Dogan T and Ece A and Akyel NG and Yuksel A},
  title = {Neurovascular Involvement in Arterial Tortuosity Syndrome Associated with a Homozygous SLC2A10 p.(Trp162Ter) Variant: Clinical, Molecular, and In Silico Characterization.},
  journal = {International journal of molecular sciences},
  year = {2026},
  doi = {10.3390/ijms27156806},
  note = {PMID: 42589462},
}
TY  - JOUR
AU  - Bozlak S
AU  - Yavas C
AU  - Yalcin E
AU  - Seflekci Y
AU  - Dogan T
AU  - Ece A
AU  - Akyel NG
AU  - Yuksel A
TI  - Neurovascular Involvement in Arterial Tortuosity Syndrome Associated with a Homozygous SLC2A10 p.(Trp162Ter) Variant: Clinical, Molecular, and In Silico Characterization.
T2  - International journal of molecular sciences
PY  - 2026
DO  - 10.3390/ijms27156806
AN  - PMID:42589462
ER  - 

摘要

Arterial Tortuosity Syndrome (ATS) is a rare autosomal recessive connective tissue disorder caused by pathogenic variants in SLC2A10, which encodes the facilitative glucose transporter GLUT10. Although its vascular features are well recognized, the molecular consequences of many truncating variants remain poorly understood. We report a patient with ATS carrying a homozygous nonsense variant, c.485G > A (p.Trp162Ter), identified by whole-exome sequencing. Quantitative real-time PCR assessed SLC2A10 expression, and integrated bioinformatic analyses (structural modeling, druggability prediction, transmembrane topology, molecular docking, and molecular dynamics) explored its structural impact. The patient presented with severe systemic arterial tortuosity, congenital cardiovascular anomalies, hernias, connective tissue abnormalities, and neurovascular involvement involving cerebral tortuosity and distal intracranial narrowing. Structural modeling revealed extensive truncation of GLUT10 and loss of multiple α-helical domains, with transmembrane helices reduced from twelve to five. Docking of nine known ligands showed weaker binding to the mutant, and Compound 892 bound most strongly to the wild type (-7.469 kcal/mol). Across 300 ns simulations, the mutant complex proved markedly less stable. qRT-PCR showed no significant transcript differences among patient, carriers, and controls. Our findings broaden the neurovascular spectrum of SLC2A10-related ATS and demonstrate that p.(Trp162Ter) severely disrupts GLUT10 architecture, topology, and ligand binding.

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